2018 Confirmed Speakers

Conference Keynote Speakers

Alison Schecter

Global Rare Diseases, External...

Sanofi Genzyme

Alvin Shih

Chief Executive Officer

Enzyvant Therapeutics

Anthony Arleth

Managing Director

Consultancy Practice, Pennside Partners Ltd.

Arndt Rolfs


Centogene AG - The Rare Disease Compa

Barry Ticho

Chief Medical Officer

Stoke Therapeutics, Inc.

Brian Bronk

Head of External Innovation, R...


Christian Girard

Co-Founder & CEO

Overlord Pharmaceuticals

Cara Blair

Client Services Director

Complete HealthVizion

David Cory

President and CEO

Eiger BioPharmaceuticals

Frédéric Honoré

Senior Manager,

Global Regulatory Affairs Portfolio Products, Alexion

Isabelle Lousada

CEO & President

Amyloidosis Research Consortium

Jodie Gillon

Global Medical Lead, Patient E...

Pfizer Inc.

Justin Bingham

Vice President of Business Dev...


Katherine Stueland

Chief Commercial Officer


Ken Kengatharan

Managing Director

Atheneos Capital and Chairman & CBO, Renexxion

Khrystal K. Davis

CEO and Patient Advocate

Zebra Leaf Publishing

Kei Kishimoto

Chief Scientific Officer

Selecta Biosciences

Leslie Leahy

VP, Medical Sciences

Ovid Therapeutics

Louise Picken

Senior Services Director

Complete HealthVizion

Lori Shafner

VP, Global Development Team Le...

Alexion Pharmaceuticals, Inc.

Luke Rosen

Patient Engagement

Ovid Therapeutics

Mahesh Kolar

Vice President, Strategy and B...

Rarity Health

Mark Krueger

Chief Strategic Officer

MK&A Inc.

Matthias P. Schönermark

Managing Director


Michael A. Swit

FDA Legal Counsel

Law Offices of Michael A. Swit

Mike Page

Executive Director

Global Regulatory Affairs Portfolio Products, Alexion

Mike Kelliher

Vice President, Business Devel...

Horizon Pharma

Nan Doyle

Senior Manager

Alnylam Pharmaceuticals

Philip J. Brooks

Program Director

Division of Clinical Innovation , NCATS, NIH

Rachelle Dixon

President / Co-Founder

HSAN1E Society

Ray Takigiku

Co-Founder, President and CEO

Bexion Pharmaceuticals, Inc.

Radhika Tripurareni

VP, Medical Affairs

Prothena Biosciences

Richard A. Basile

Co Founder and CEO

BioPontis Alliance for Rare Diseases

Robert (bob) Ward

Chairman, Chief Executive Offi...

Eloxx Pharmaceuticals

Sabrina Mogle

Co-Founder and CEO

RareMoon, Orphan Drug Regulatory Services

Stephan Toutain

SVP, Operations

Anavex Life Sciences

Tim Miller

Co-Founder, President and Chie...

Abeona Therapeutics

Toby Freyman

Senior Director, Business Deve...


Vikram Karnani

Executive VP, Chief Commercial...

Horizon Pharma

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Tel. +44 203 567 1321

Tel. +44 203 567 1321

Tel. +44 203 567 1321