Featuring

11th Orphan Drugs & Rare Diseases Global Congress 2019 Americas

Days
Hours
Minutes
Seconds

9th September 2019 - Pre-Conference Workshop
10th - 11th September 2019 - 2 Days Conference
Boston, MA, USA

Venue

Hilton Boston Back Bay

Address

40 Dalton St, Boston, MA 02115

Phone

(617) 236-1100

Pharma Conference US Boston

Orphan Drugs & Rare Diseases

Paradigm Global Events is again proud to present our Orphan Drugs and Rare Diseases Global Congress 2019 Americas. It’s the 11th in the series of our Flagship tri-annual Orphan Drugs and Rare Diseases event, this congress will provide you with current trends and innovations driving access to meet unmet medical needs of rare disease patients.

Introducing a new format this year, we are putting together an agenda that addresses “Current Trends and Innovations driving access to meet unmet medical needs of rare disease patients”.
We have gathered together 50+, high caliber expert speakers to participate and share their knowledge and expertise through Panel discussions, keynote presentations, round table discussions and 4 major agenda streams addressing all aspect of the industry.

From a patient advocacy organization perspective, was a very informative meeting. Learned a lot from presentations and networking that will inform how we can add value to the advocacy-patient-drug developer dialogue.

aftd
Dr. Nadine Tutton

Scientific Director, Research, Association for Frontotemporal Degeneration

I was very impressed with the format, the content was interesting and well done. I felt I learned a lot and was glad to be able to attend.

pharmolam
Senior Director

Business Development at Pharm-Olam, LLC

Introducing

NEW 2019 CONFERENCE FORMAT

New for Orphan Drugs & Rare Diseases Global Congress 2019 – choose your focus streams in the afternoon of both conference days by attending keynotes, presentations and group discussions that have the most relevance to you. Choose from..

Regulatory, Commercial & Current Trends

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Regulatory, Commercial & Current Trends

This focus stream covers improving the precision of precision medicines, understanding technical issues, novel approaches to regulation, the role of patient organizations in approval, pricing, reimbursement and more!

Access and Collaborations

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Access and Collaborations

This focus stream highlights global early access programs to support rare indications, the importance of Latin American sponsors with Orphan Disease Therapies, utilizing real-world evidence and more!

Innovations, Discovery & Clinical Development

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Innovations, Discovery & Clinical Development

This focus stream explores the rare disease final frontier and whether Asia is the place where innovation will be found in the 2020's. We also explore Hermansky-Pudlak Syndome, drugs development resources and much more.

Advance Therapy Medicinal Products

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Advance Therapy Medicinal Products

This focus stream explores advance therapies and their promises/potentials for rare disease, novel approaches for development of Hybrid Cell Therapies, the NIH Common Fund Somatic Cell Genome Editing Program and more!

Gold Sponsor

Gold Sponsor

Gold Sponsor

Silver Sponsor

Bronze Sponsor

Lead Exhibitor

Associate Sponsor