Previously Featured Speakers
18th Orphan Drugs & Rare Diseases Global Congress 2022 Americas
- Rogerio Vivaldi, M.D., M.B.A., President and Chief Executive Officer, Sigilon Therapeutics Inc.
- Sonal Bhatia, Chief Medical Officer, Rare Disease, Pfizer
- Melinda Bachini, Director of Advocacy, Cholangiocarcinoma Foundation
- Alan J. Balch, PhD.,CEO, National Patient Advocate Foundation
- Rahul Ballal, PhD, President & CEO, Imara Inc.
- Tara J. Britt, Founder and President, Rare Disease Innovations Institute, Inc.
- Philip J. Brooks, PhD, Program Director, Office of Rare Diseases Research, NCATS, NIH
- Deborah Collyar, President, Patient Advocates In Research (PAIR)
- Christopher Dandrea, Vice President, Global Program Management, uniQure
- Khrystal Davis, Founder, Texas Rare Alliance
- Scott Dorfman, CEO, Odylia Therapeutics
- Wendy Erler, Head of Patient Experience and Insights, Alexion Pharmaceuticals, Inc.
- Clasina Field, Co-Executive Director, Bensfriends.org
- Andrea C. Furia-Helms, M.P.H., Director, Patient Affairs Staff, Office of Clinical Policy and Programs, Office of the Commissioner, U.S. Food and Drug Administration
- Dr Femida Gwadry-Sridhar, Founder & CEO, Pulse Infoframe
- Angela Ramirez Holmes, Founder/President, CA Action Link for Rare Diseases (Cal Rare)
- Lisa Kearns, MS, MA., Division of Medical Ethics, NYU Grossman School of Medicine
- Tom James Lambdin, Co-Executive Director, Bensfriends.org
- Debra Miller, Chief Executive Officer/Founder, CureDuchenne
- Neena Nizar, President & Founder, The Jansens Foundation
- David A Pearce, PhD, President of Innovation, Research, & World Clinic, Sanford Health
- Mike Page, VP, Head of Global Regulatory Affairs Development Strategy, Alexion Pharmaceuticals, Inc.
- Luke Rosen, VP, Accelerated Development & Community Engagement, Ovid Therapeutics
- Christine Von Raesfeld, Founder & CEO, People with Empathy
- Samuel L. Seward, Jr., MD, FACP, Professor and Chair, Mount Sinai Morningside and Mount Sinai West Department of Medicine
- Haya Taitel, Senior Vice President, Chief Commercial Officer, Kadmon
- Barry Ticho, M.D., PhD., Chief Medical Officer, Stoke Therapeutics, Inc.
- Cherry T. Thomas, M.D., SVP Clinical Development, Caribou Biosciences, Inc.
- Monica L Weldon, President/CEO/Founder, Bridge The Gap - SYNGAP ERF
- Simu Thomas PhD, Vice President, Global Head HEOR, Alexion Pharmaceuticals
- Karmen Trzupek, Director, Clinical Trial Services, InformedDNA
- Tara J. Britt, Founder and President, Rare Disease Innovations Institute, Inc.
- Robert Donnell, Executive Vice President – Medicines Access, Smartway Pharma, a leading provider of Early / Expanded Access Programs (EAP).
- Kristin Smedley, President, Curing Retinal Blindness Foundation
- And many more...